129 Participants NeededMy employer runs this trial

Ferumoxytol for Iron-Deficiency Anemia

Recruiting at 25 trial locations
CT
Overseen ByClinical Trial Interest
No Placebo GroupAll trial participants will receive the active study treatment (no placebo)
Pivotal Trial (Near Approval)This treatment is in the last trial phase before FDA approval
Prior Safety DataThis treatment has passed at least one previous human trial

What You Need to Know Before You Apply

What is the purpose of this trial?

This trial tests a new iron treatment called ferumoxytol for children with iron deficiency anemia (IDA) and chronic kidney disease (CKD). Researchers aim to determine if ferumoxytol is safe and more effective than iron sucrose. The study also examines how the body processes ferumoxytol. Children who may qualify for this trial have CKD, low iron levels, and have not responded to oral iron treatments. As a Phase 3 trial, this study represents the final step before FDA approval, offering participants an opportunity to contribute to potentially groundbreaking treatment advancements.

Do I have to stop taking my current medications for the trial?

The trial information does not specify if you need to stop taking your current medications. It's best to discuss this with the trial coordinators or your doctor.

Is there any evidence suggesting that this trial's treatments are likely to be safe?

Research has shown that ferumoxytol is generally well-tolerated, though some side effects have been observed. Most side effects occurred within 48 hours after treatment and included dizziness and low blood pressure. Importantly, no life-threatening or fatal incidents were reported. While ferumoxytol can cause serious allergic reactions, these are rare.

Iron sucrose, the comparator in this study, has been used for a long time and is generally considered safe. Overall, both ferumoxytol and iron sucrose have shown good tolerance, but like any treatment, they carry potential risks, particularly related to allergic reactions.12345

Why do researchers think this study treatment might be promising for CKD?

Ferumoxytol is unique because it offers a new approach to treating iron deficiency anemia (IDA) in kids with chronic kidney disease (CKD). Unlike traditional treatments like iron sucrose, ferumoxytol is an iron oxide nanoparticle that can be administered quickly, potentially reducing the number of hospital visits. Researchers are excited because its fast infusion time and potential for fewer side effects could make managing anemia easier and more comfortable for young patients.

What evidence suggests that this trial's treatments could be effective for pediatric CKD subjects with iron deficiency anemia?

Research has shown that ferumoxytol, one of the treatments studied in this trial, effectively treats iron deficiency anemia (IDA), especially when oral iron supplements are ineffective or unsuitable. Studies have found that ferumoxytol can increase hemoglobin levels, which are crucial for oxygen transport in the blood. One study showed it was more effective than iron sucrose at raising hemoglobin levels in patients. Participants in this trial may receive either ferumoxytol or iron sucrose, the latter being another treatment option under study. Those receiving ferumoxytol have experienced significant improvements in their iron levels. Overall, ferumoxytol appears to be a strong treatment option for individuals with IDA, particularly those with chronic kidney disease (CKD).678910

Are You a Good Fit for This Trial?

This trial is for children with chronic kidney disease who have iron deficiency anemia or are at risk of it. Participants must have tried and not tolerated oral iron, or can't take it. They need to meet certain blood test levels and use birth control if sexually active. Those with severe allergies to IV iron, very low blood pressure, or high ferritin can't join.

Inclusion Criteria

Has Chronic Kidney Disease defined as one of the following: on chronic hemodialysis; receiving chronic peritoneal dialysis; estimated glomerular filtration rate (eGFR) of <60 mL/min/1.73 m2; has evidence of structural and/or functional abnormalities e.g., persistent albuminuria, abnormal urine sediment, electrolyte and other abnormalities due to tubular disorders for > 3 months.
For patients other than hemodialysis dependent CKD patients, documented history of unsatisfactory oral iron therapy or in whom oral iron cannot be tolerated, or for whom oral iron is considered medically inappropriate
All subjects (female and male) of childbearing potential who are sexually active must be on an effective method of birth control for at least 1 month prior to Day 1 Dosing and agree to remain on birth control until completion of the study
See 1 more

Exclusion Criteria

Known hypersensitivity reaction to any component of ferumoxytol and iron sucrose
You have had an allergic reaction to IV iron in the past.
You have had allergic reactions to more than two different medications in the past.
See 3 more

Timeline for a Trial Participant

Screening

Participants are screened for eligibility to participate in the trial

2 weeks

Treatment

Participants receive either ferumoxytol or iron sucrose for the treatment of iron deficiency anemia

5 weeks
Multiple visits for IV infusions

Follow-up

Participants are monitored for safety and effectiveness after treatment

2 weeks

What Are the Treatments Tested in This Trial?

Interventions

  • Ferumoxytol
  • Iron Sucrose

Trial Overview

The study compares two intravenous (IV) treatments for iron deficiency anemia in kids with chronic kidney disease: ferumoxytol versus the standard treatment, iron sucrose. The goal is to see which works better and is safer.

How Is the Trial Designed?

2

Treatment groups

Experimental Treatment

Active Control

Group I: FerumoxytolExperimental Treatment1 Intervention
Group II: Iron sucroseActive Control1 Intervention

Ferumoxytol is already approved in United States, European Union, Canada for the following indications:

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Approved in United States as Feraheme for:
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Approved in European Union as Feraheme for:
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Approved in Canada as Feraheme for:

Find a Clinic Near You

Who Is Running the Clinical Trial?

AMAG Pharmaceuticals, Inc.

Lead Sponsor

Trials
44
Recruited
11,300+

Citations

Efficacy and safety of IV ferumoxytol for adults with iron ... - PMC

Ferumoxytol was effective and well tolerated in patients with IDA of any underlying cause in whom oral iron was ineffective or could not be used.

FERAHEME® vs Placebo | Comparative efficacy & safety

FERAHEME is the only IV iron with patient-reported outcome data in the label1. In IDA Trial 1 and the extension trial, just 1 gram of FERAHEME demonstrated: ...

Efficiency Outcomes Associated with Increased Ferumoxytol ...

The clinic estimates that 80% of patients receiving IV iron treatment have reduced kidney function. Ferumoxytol treatment became available in ...

Evaluation of Single-Dose Intravenous Infusions ...

The primary efficacy endpoint of the analysis included median changes from baseline in hemoglobin, hematocrit, and ferritin levels 8 to 12 weeks ...

A Phase III, randomized, open-label trial of ferumoxytol ... - PMC

Ferumoxytol was shown to be superior to iron sucrose in the mean increase in Hgb from Baseline to Week 5 (the alternate, preplanned primary efficacy endpoint), ...

Safety and side effects | FERAHEME® (ferumoxytol injection)

Safety and side effects of FERAHEME® in ~2000 iron deficiency anemia patients, including rates of hypersensitivity and hypotension. See Boxed Warning.

Safety Data Sheet (SDS)

Do not take action without suitable protective clothing - see section 8 of SDS. Evacuate personnel to safe areas. Ensure adequate ventilation.

What Does the Boxed Warning Tell Us? Safe Practice of Using ...

Most AEs occurred within 48 hours after ferumoxytol infusion (in 58 cases [8.6% of the infusions]). There were no life-threatening or fatal (grade 4 or 5) AEs.

MSDS

In clinical trials, patients treated intravenously with high doses of ferumoxytol experienced gastrointestinal effects, dizziness, hypotension ...

Feraheme. - accessdata.fda.gov

Risk Summary. Limited available data with ferumoxytol use in pregnant women are insufficient to inform a drug associated risk of adverse developmental outcomes.