179 Participants Needed

Rapcabtagene Autoleucel for Lupus Nephritis

Recruiting at 88 trial locations
NP
Overseen ByNovartis Pharmaceuticals
Age: 18+
Sex: Any
Trial Phase: Phase 2
Sponsor: Novartis Pharmaceuticals
No Placebo GroupAll trial participants will receive the active study treatment (no placebo)
Prior Safety DataThis treatment has passed at least one previous human trial

What You Need to Know Before You Apply

What is the purpose of this trial?

This trial tests rapcabtagene autoleucel, an anti-CD19 chimeric antigen receptor T cell therapy, to help people with lupus nephritis, a kidney condition caused by systemic lupus erythematosus (SLE). The trial aims to evaluate the treatment's effectiveness and safety for those who have not responded to at least two other therapies. Suitable candidates for this trial have active lupus nephritis, struggle to control their symptoms, and possess specific lupus-related antibodies in their blood. As a Phase 2 trial, the research focuses on assessing the treatment's effectiveness in an initial, smaller group of participants.

Will I have to stop taking my current medications?

The trial mentions an 'immunosuppressive washout' period, which suggests you may need to stop taking certain medications that suppress the immune system before participating. However, the protocol does not specify which medications or how long the washout period is.

Is there any evidence suggesting that rapcabtagene autoleucel is likely to be safe for humans?

Research has shown that rapcabtagene autoleucel, a new type of CAR-T cell therapy, shows promise in studies. Early results suggest it is well-tolerated by patients with systemic lupus erythematosus (SLE), a long-term autoimmune disease. Administered once after a procedure called lymphodepletion, this therapy prepares the body for treatment.

While researchers continue to gather information about its effects on lupus nephritis (a kidney problem related to SLE), the overall safety profile of rapcabtagene autoleucel appears positive. Any side effects reported so far have been manageable. As the treatment undergoes further testing, researchers are closely monitoring for any unexpected issues. However, the results so far are encouraging for those considering joining a trial.12345

Why do researchers think this study treatment might be promising for lupus nephritis?

Unlike the standard treatments for lupus nephritis, which usually involve immunosuppressive drugs and steroids, rapcabtagene autoleucel is an innovative approach that uses a patient's own immune cells to fight the disease. This treatment is a form of CAR-T cell therapy, where T cells are engineered to specifically target and attack the cells causing harm in lupus nephritis. Researchers are excited about this therapy because it has the potential to provide long-lasting remission by addressing the root cause of the condition, rather than just managing symptoms. This could mean fewer side effects and a more sustainable treatment option for patients.

What evidence suggests that rapcabtagene autoleucel might be an effective treatment for lupus nephritis?

Research has shown that rapcabtagene autoleucel, the treatment under study in this trial, may hold promise for treating lupus nephritis. Early data suggest it is safe and effective in increasing CAR T-cells, which help reduce B-cells involved in lupus. These initial findings indicate it might work well for managing severe, hard-to-treat cases of systemic lupus erythematosus, closely linked to lupus nephritis. Although more research is needed, these results offer hope for those seeking new treatment options.12345

Who Is on the Research Team?

NP

Novartis Pharmaceuticals

Principal Investigator

Novartis Pharmaceuticals

Are You a Good Fit for This Trial?

This trial is for people with active, hard-to-treat lupus nephritis—a kidney condition caused by systemic lupus erythematosus. Participants should have tried other treatments without success. Specific criteria for joining or reasons to be excluded aren't provided here.

Inclusion Criteria

SLEDAI-2K Criteria at screening: SLEDAI-2K score >= 6 points (Gladman et al 2002, Touma et al 2011), excluding points attributed to 'fever', 'lupus headache', 'alopecia', and 'organic brain syndrome'
I have active lupus affecting my kidneys without long-term damage.
I have tried at least two treatments for my condition without success.
See 1 more

Exclusion Criteria

I do not have a severe lupus flare that needs immediate treatment beyond pulse GCs.
I have hepatitis B or C.
I have signs of active or latent tuberculosis.
See 5 more

Timeline for a Trial Participant

Screening

Participants are screened for eligibility to participate in the trial

Up to 6 weeks

Treatment

Participants are randomized to receive either rapcabtagene autoleucel or Standard of Care (SOC) for systemic lupus erythematosus with active, refractory lupus nephritis

104 weeks

Follow-up

Participants are monitored for safety and effectiveness after treatment

Up to 104 weeks

Long-term follow-up

Participants who received rapcabtagene autoleucel infusion will enter a long-term follow-up period

Up to 15 years

What Are the Treatments Tested in This Trial?

Interventions

  • Rapcabtagene Autoleucel
Trial Overview The study tests two different dosing regimens of a new therapy called rapcabtagene autoleucel against the standard treatment for lupus nephritis. It aims to see if this new approach is more effective and safe compared to what's currently used.
How Is the Trial Designed?
1Treatment groups
Experimental Treatment
Group I: rapcabtagene autoleucelExperimental Treatment1 Intervention

Find a Clinic Near You

Who Is Running the Clinical Trial?

Novartis Pharmaceuticals

Lead Sponsor

Trials
2,963
Recruited
4,275,000+
Founded
1996
Headquarters
Basel, Switzerland
Known For
Precision medicine
Top Products
Gleevec, Cosentyx, Entresto, Kisqali
Dr. Vas Narasimhan profile image

Dr. Vas Narasimhan

Novartis Pharmaceuticals

Chief Executive Officer since 2018

MD from Harvard Medical School

Dr. Shreeram Aradhye profile image

Dr. Shreeram Aradhye

Novartis Pharmaceuticals

Chief Medical Officer since 2021

MD

Published Research Related to This Trial

Cyclophosphamide (CYC) is still the first-choice treatment for severe proliferative lupus nephritis, despite the availability of newer treatment options.
There is ongoing debate regarding the optimal route, dosage, and duration of CYC therapy, highlighting the need for further research to refine treatment protocols.
Lupus nephritis: current issues.Mavragani, CP., Moutsopoulos, HM.[2019]
In a study of 31 patients with systemic lupus erythematosus (SLE) who had active nephritis or autoimmune cytopenias, the addition of anti-CD20 treatment (rituximab) led to complete B cell depletion and significant clinical improvements, including increased glomerular filtration rate (GFR) in 11 out of 17 nephritis patients.
The treatment was particularly effective for autoimmune thrombocytopenia, with significant increases in platelet counts observed within one month, and five out of ten patients achieving complete normalization of their platelet counts within six months.
Longterm clinical and immunological effects of anti-CD20 treatment in patients with refractory systemic lupus erythematosus.Lindholm, C., Börjesson-Asp, K., Zendjanchi, K., et al.[2022]
In a small study of five treatment-resistant patients with systemic lupus erythematosus (SLE), CD19 CAR T cell therapy led to significant clinical improvements and remission in all participants after 3 months, demonstrating its potential efficacy.
The treatment was well tolerated, with only mild cytokine release syndrome reported, suggesting a favorable safety profile for this innovative therapy in seriously ill SLE patients.
Journal Club: Anti-CD19 Chimeric Antigen Receptor T Cell Therapy for Refractory Systemic Lupus Erythematosus.Boulougoura, A., Gendelman, H., Surmachevska, N., et al.[2023]

Citations

NCT06581198 | A Study of Rapcabtagene Autoleucel in ...The purpose of this study is to evaluate the efficacy and safety of rapcabtagene autoleucel (administered once following lymphodepletion) in patients with ...
pos0046 preliminary results of an open-label, multicentre ...Conclusion: Preliminary data from this clinical trial suggest favourable safety, CAR T-cell expansion, B-cell depletion and initial efficacy of YTB323 in srSLE, ...
Novartis showcases significant immunology advancements ...Additional presentations include data for rapcabtagene autoleucel, a novel one-time investigational CAR-T cell therapy being evaluated across ...
A Study of Rapcabtagene Autoleucel in Active, Refractory ...A Phase 2, Open-label, Study to Evaluate the Efficacy and Safety of Rapcabtagene Autoleucel in Patients With Active, Refractory Systemic Lupus Erythematosus ( ...
NCT05798117 | An Open-label, Study to Assess Safety, ...The study is intended to assess safety, efficacy and cellular kinetics of YTB323 treatment in participants with severe refractory systemic lupus erythematosus.
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